▲ Peaking
Science
Gene therapy that led to boy’s death had limited efficacy
Recent coverage examines a fatal gene-editing trial in China that showed limited efficacy alongside severe safety concerns.
Duchenne Muscular Dystrophy
2 trends tracked about this subject — the full history, oldest to newest below.
◼ Archived
Business
🔮 fades ✗
Ahead of hearing, FDA questions the efficacy of Capricor’s Duchenne drug
FDA scientists are disputing efficacy claims regarding Capricor Therapeutics' Phase 3 Duchenne muscular dystrophy cell therapy, triggering a stock plunge.