4 trends tracked about this subject — the full history, oldest to newest below.
Personalized gene therapy using bespoke ASOs has enabled a teen with SCN2A-related epileptic encephalopathy to walk independently for the first time.
Anthropic is aggressively entering the biopharma sector through a 100-day sprint involving Nobel laureates, M&A activity, and new scientific AI tools.
A $160 million non-profit initiative in Boston aims to revolutionize the development of genetic medicines for rare and ultra-rare diseases.
Hollywood icon Tyler Mane’s breast cancer diagnosis sparks rare male health awareness