7 trends tracked about this subject — the full history, oldest to newest below.
A one-year-old baby has undergone a world-first surgery utilizing super-elastic springs to treat a rare condition involving a fused skull.
An accelerator backed by the RK Mellon Foundation aims to tackle rare diseases lacking approved drugs.
U.S. public health faces severe tests from rare disease outbreaks amid funding cuts and vaccine resistance.
Personalized gene therapy using bespoke ASOs has enabled a teen with SCN2A-related epileptic encephalopathy to walk independently for the first time.
Anthropic is aggressively entering the biopharma sector through a 100-day sprint involving Nobel laureates, M&A activity, and new scientific AI tools.
A $160 million non-profit initiative in Boston aims to revolutionize the development of genetic medicines for rare and ultra-rare diseases.
Hollywood icon Tyler Mane’s breast cancer diagnosis sparks rare male health awareness